Shares of Neurogene rose after the Food and Drug Administration granted breakthrough therapy designation to its NGN-401 therapy to treat Rett Syndrome. The stock jumped 36% to $26.83 in Friday's ...
FDA grants Breakthrough Therapy designation to luvesilocin for postpartum depression following positive results from the phase 2 RECONNECT trial.
UCLA researchers use lipid nanoparticles to insert full CFTR gene into airway cells, restoring function and opening new ...
Neurogene received FDA Breakthrough Therapy Designation for NGN-401 in Rett Syndrome, driving a >25% share price surge. Click ...
Nomlabofusp program granted Breakthrough Therapy Designation for the treatment of adults and children with FA based on FDA’s ...
Pritelivir, an investigational antiviral drug for herpes simplex virus, demonstrated “superior efficacy” in healing lesions ...
Larimar on Tuesday said nomlabofusp, a protein replacement therapy that is being developed as a potential treatment for Friedreich's ataxia, was granted the important designation that is designed to ...
Forget Vertex Pharmaceuticals -- CRISPR Therapeutics is a better buy right now.
High dose and low dose AMT-130 demonstrated an 80% and 30% slowing of disease progression vs external control, respectively. The Food and Drug Administration has granted Breakthrough Therapy ...
Nipocalimab 15mg/kg improved ClinESSDAI score compared with placebo (treatment difference -2.65; [90% CI, -4.03, -1.28]; P =.002). The Food and Drug Administration (FDA) has granted Breakthrough ...
The FDA granted breakthrough therapy designation to Rybrevant Faspro based on data from the phase 1b/2 OrigAMI-4 study (NCT06385080).
Forty-Hz auditory stimulation increased amyloid clearance markers in aged primates and produced lasting effects, supporting ...
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